Designing and Developing LNP Characterization Techniques for Gene Editing Delivery
Time: 2:45 pm
day: Day Two
Details:
- Discussing standard characterization techniques to determine size, PDI, cargo concentration, morphology, LNP concentration, and encapsulation efficiency
- Understanding in vitro and in vivo potency to determine the efficacy of the delivery vehicle
- Developing advanced characterization techniques to determine cargo instability, and structure-activity relationships